Cell therapy for Duchenne muscular dystrophy: promises, challenges, and controversies

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Cell therapy shows promise for treating duchenne muscular dystrophy, though it is not yet clinically validated.
Key metrics highlight poor cell engraftment and low delivery efficiency as significant hurdles in treatment strategies.
The review assesses various cell types, including muscle satellite cells and iPSC-derived muscle cells, as potential solutions.
Safety concerns, particularly around tumorigenicity and immune rejection, warrant rigorous evaluation before adoption.

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This review discusses cell therapy's potential for treating Duchenne muscular dystrophy, highlighting challenges with safety and efficacy.

Łoboda et al. (2025) studied this question.

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This review discusses cell therapy's potential for treating Duchenne muscular dystrophy, highlighting challenges with safety and efficacy.